华东医药旗下珲信生物与尧唐生物达成战略合作
华东医药(股票代码:000963)旗下控股子公司杭州珲信生物科技有限公司(简称“珲信生物”)与尧唐(上海)生物科技有限公司(简称“尧唐生物”)在杭州签署战略合作协议
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华东医药(股票代码:000963)旗下控股子公司杭州珲信生物科技有限公司(简称“珲信生物”)与尧唐(上海)生物科技有限公司(简称“尧唐生物”)在杭州签署战略合作协议
2023年6月8日,由生物经纬主办的“经纬药说”主题沙龙第40期在南京江北新区BioMatrix Center孵化器举行,本期主题百舸争流千帆竞,基因治疗谁为先。
Fu, B., Liao, J., Chen, S., Li, W., Wang, Q., Hu, J., Yang, F., Hsiao, S., Jiang, Y., Wang, L., Chen, F., Zhang, Y., Wang, X., Li, D., Liu, M., &Wu, Y.2022. CRISPR-Cas9-mediated gene editing of the BCL11A enhancer for pediatric beta(0)/beta(0) transfusion-dependent beta-thalassemia.Nat Med, 28: 1573–1580.
Demirci, S., Zeng, J.,Wu, Y., Uchida, N., Shen, A. H., Pellin, D., Gamer, J., Yapundich, M., Drysdale, C., Bonanno, J., Bonifacino, A. C., Krouse, A. E., Linde, N. S., Engels, T., Donahue, R. E., Haro-Mora, J. J., Leonard, A., Nassehi, T., Luk, K., Porter, S. N., Lazzarotto, C. R., Tsai, S. Q., Weiss, M. J., Pruett-Miller, S. M., Wolfe, S. A., Bauer, D. E., & Tisdale, J. F. 2020. BCL11A enhancer-edited hematopoietic stem cells persist in rhesus monkeys without toxicity.J Clin Invest, 130(12): 6677-6687.
Zeng, J.,Wu, Y., Ren, C., Bonanno, J., Shen, A. H., Shea, D., Gehrke, J. M., Clement, K., Luk, K., Yao, Q., Kim, R., Wolfe, S. A., Manis, J. P., Pinello, L., Joung, J. K., & Bauer, D. E. 2020. Therapeutic base editing of human hematopoietic stem cells.Nat Med, 26(4): 535-541.
Zhang, X., Chen, L., Zhu, B., Wang, L., Chen, C., Hong, M., Huang, Y., Li, H., Han, H., Cai, B., Yu, W., Yin, S., Yang, L., Yang, Z., Liu, M., Zhang, Y., Mao, Z.,Wu, Y., Liu, M., & Li, D. 2020a. Increasing the efficiency and targeting range of cytidine base editors through fusion of a single-stranded DNA-binding protein domain.Nat Cell Biol, 22(6): 740-750.
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